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Treatments for Transthyretin Amyloidosis (ATTR)
Transthyretin Amyloidosis (ATTR) Treatments Webinar, January 18, 2025 presented by Amyloidosis Support Groups.
Moderator
Muriel Finkel, President, Amyloidosis Support Groups
Speakers
Chafic Karam, MD, Chief, Neuromuscular Division, Professor of Neurology, Penn Amyloidosis Center, University of Pennsylvania, Philadelphia, PA
Farooq Sheikh, MD, Medical Director, Advanced Heart Failure Program, MedStar Heart and Vascular Institute, Associate Professor of Medicine, Georgetown University School of Medicine, Washington, DC
Brett Sperry, MD, Director, Cardiac Amyloidosis Program, Saint Luke's Mid America Heart Institute, Assistant Professor of Medicine, University of Missouri, Kansas City, MO
Frederick L. Ruberg, MD, Chief for Cardiovascular Medicine, Boston University Medical Center, Professor of Medicine, Boston University School of Medicine, Boston, MA
Paula Schmitt, Executive Director, Amyloidosis Support Groups
Chapters
0:00 Introduction
4:51 Dr. Farooq Sheikh: Disease Modifying Therapies for Transthyretin Cardiac Amyloidosis
21:17 Dr. Brett Sperry: Curing ATTR-CM: Are We Getting Closer?
37:59 Dr. Chafic Karam: Polyneuropathy Treatments for Hereditary ATTR
54:15 Paula Schmitt: Financial Assistance
1:04:44 Question and Answer Session, Drs. Karam, Sheikh, Sperry, Ruberg
LINKS REFERENCED IN WEBINAR
Therapies for ATTR in 2025: https://drive.google.com/file/....d/115w2QgJLEMGJtCv-b
Financial Assistance Chart for 2025: https://drive.google.com/file/....d/1-1bng5jSCr9Fn0D0u
PHARMA Websites for Assistance and Information
www.AlnylamAssist.com
www.vyndalink.com - 1-888-222-8475 8 am -8 pm
Attruby - https://forgingbridges.com/patient/financial/
Vyndamax In Canada https://www.pfizer.ca/en/our-p....roducts/assistance-p
https://www.myaccess360.com/pa....tient/wainua-eplonte
ATTR Financial Assistance
https://fundfinder.panfoundation.org/
www.panfoundation.org
www.tafcares.org
www.copays.org
https://rarediseases.org/patie....nt-assistance-progra
www.healthwellfoundation.org - their cardiomyopathy fund covers Attruby
Free Genetic Testing
Alnylam Act and Prevention Genetics: https://www.preventiongenetics.....com/sponsoredTestin
Astra Zeneca/Ionis and Prevention Genetics: https://www.preventiongenetics.....com/sponsoredTestin
This webinar video has been edited for content and time.
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