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Past, Present, and Future Treatment Options for Desmoid Tumors

4 Tampilan • 06/28/23
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Mary Smith, PhD, of SpringWorks Therapeutics explains the past, present, and future treatment options for Desmoid tumors.

Desmoid tumors are benign soft tissue tumors that can invade surrounding tissues, suchas joints, muscle and viscera. Historically, treatment was limited to surgery and/or watchful waiting, but new therapies are in development, such as SpringWorks nirogacestat.

Nirogacestat is a gamma secretase inhibitor currently being investigated in a Phase 3 clinical trial involving adults and a Phase 2 clinical study involving children with Desmoid tumors.

To stay abreast of the latest developments in Desmoid tumors and other rare conditions, sign up to our weekly newsletter at checkrare.com/sign-up/

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